A new drug therapy is showing remarkable results in patients with cystic fibrosis, according to a new study, alleviating symptoms and attacking the genetic root of the disease.
Researchers say that the new drug combination could benefit up to 90 percent of those who have the disease, something that has not been seen before, according to a story from the Washington Post.
Cystic fibrosis causes a buildup of thick mucus in the lungs and other organs and often kills those with the disease when they are in their teens.
The Cystic Fibrosis Foundation called the FDA's approval a "tremendous breakthrough" for patients. Around 30,000 people in the United States have cystic fibrosis, according to the CF Foundation.
Around half of those people are age 18 or older.
Francis Collins, the director of the National Institutes of Health, said the discovery was a "cause for celebration." Collins was part of the team that 30 years ago discovered the gene that mutates and causes the disease.
Dr. Jeffrey Leiden, the chairman of Vertex Pharmaceuticals, said the drug therapy "corrects the function of a mutant protein" that causes the disease.
The new drug therapy comes with a high price tag. According to Vertex, the therapy will cost $311,000 a year.
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